Citations 2
C9orf72 BAC Transgenic Mice Display Typical Pathologic Features of ALS/FTD (P4.001)
Baloh, Robert H. , O’Rourke, Jacqueline G., Bell, Shaughn , Bogdonik, Laurent, Muhammad, AKMG, Austin, Andrew D. , Cady, Janet, Liu, Elaine, Zarrow, Jonah E. , Grant, Sharday, Ho, Ritchie , Carmona, Sharon, Simpkinson, Megan, Wu, Kathryn , Daughrity, Lillian M. , Harms, Matthew , Petrucelli, Leonard , Gendron, Tania F. , Kim, Kevin , Austin, Andrew, Dickson, Dennis W. , Harms, Matthew B. , Lutz, Cathleen M.
Neurology | December 7, 2023 | Volume: 86 | Issue: 16_supplement | Pages: No page available
Targeting RNA Foci in iPSC-Derived Motor Neurons from ALS Patients with a C9ORF72 Repeat Expansion
O’Rourke, Jacqueline G., Meera, Pratap , Muhammad, A.K.M. Ghulam, Grant, Sharday, Simpkinson, Megan, Bell, Shaughn , Carmona, Sharon, Ornelas, Loren, Sahabian, Anais , Petrucelli, Leonard , Baughn, Michael W. , Ravits, John , Harms, Matthew B. , Rigo, Frank , Bennett, C. Frank , Otis, Thomas S. , Svendsen, Clive N. , Baloh, Robert H. , Sareen, Dhruv , Gendron, Tania F.
Science Translational Medicine | October 23, 2013 | Volume: 5 | Issue: 208 | Pages: No page available
Antisense oligonucleotides can correct disease-specific phenotypes in cultured motor neurons differentiated from iPSCs derived from ALS patients with a C9ORF72 repeat expansion.