Citations 1
Persistent Effect of Arimoclomol in Patients with Niemann-Pick Disease Type C: 24-Month Results from an Open-Label Extension of a Pivotal Phase 2/3 Study
Mengel, Eugen , Riol, Rosalia Maria Da, Grünewald, Stephanie , Harmatz, Paul , Héron, Bénédicte , Maier, Esther M. , Roubertie, Agathe , Santra, Saikat , Day, Simon , Andreasen, Anne Katrine, Geist, Marie Aavang, Petersen, Nikolaj H.T., Ingemann, Linda, Hansen, Thomas Michael, Blaettler, Thomas , Kirkegaard, Thomas , Dali, Christine í, Patterson, Marc C. , Toro, Mireia del , Deodato, Federica , Gautschi, Matthias , Grønborg, Sabine , Tylki‐Szymańska, Anna , Hansen, Thomas
Neuropediatrics | November 17, 2021 | Volume: No volume available | Issue: No issue available | Pages: No page available
