Citations 6
Inotersen Improves Norfolk Quality of Life-Diabetic Neuropathy Measures in Patients With Hereditary Transthyretin Amyloidosis with Polyneuropathy in the Phase 3 Study NEURO-TTR (S5.006)
Polydefkis, Michael , Coelho, Teresa , Dyck, P. James B. , Scheinberg, Morton , Brannagan, Thomas H., Whelan, Carol , Drachman, Brian, Gane, Edward , Gorevic, Peter D., Monia, Brett P. , Hughes, Steven G. , Kwoh, Jesse, McEvoy, Bradley, Ackermann, Elizabeth J., Benson, Merrill D., Wang, Annabel K., Waddington‐Cruz, Márcia , Planté‐Bordeneuve, Violaine , Berk, John L. , Barroso, Fábio , Adams, David , Merlini, Giampaolo , Heitner, Stephen B. , Conceição, Isabel , Schmidt, Hartmut , Vita, Giuseppe , Gámez, Josep , Oliveira, Acary Souza Bulle de , Baker, Brenda F. , Gertz, Morie A.
Neurology | December 7, 2023 | Volume: 90 | Issue: 15_supplement | Pages: No page available
Burden of Hereditary Transthyretin Amyloidosis With Polyneuropathy in Patients Enrolled in the Phase 3 Study NEURO-TTR (P1.331)
Wang, Annabel K., Coelho, Teresa , Polydefkis, Michael , Dyck, P. James B. , Scheinberg, Morton , Brannagan, Thomas H., Whelan, Carol , Drachman, Brian, Gane, Edward , Gorevic, Peter D., Monia, Brett P. , Hughes, Stephen G. , Kwoh, Jesse, McEvoy, Bradley, Ackermann, Elizabeth J., Guthrie, Spencer , Benson, Merrill D., Berk, John L. , Waddington‐Cruz, Márcia , Planté‐Bordeneuve, Violaine , Barroso, Fábio , Adams, David , Heitner, Stephen B. , Conceição, Isabel , Schmidt, Hartmut , Vita, Giuseppe , Gámez, Josep , Oliveira, Acary Souza Bulle de , Hughes, Stephen G., Baker, Brenda F. , Kessler, Asia Sikora , Gertz, Morie A. , Merlini, Giampaolo
Neurology | December 7, 2023 | Volume: 90 | Issue: 15_supplement | Pages: No page available
Open Label Extension of the Phase 3 Study NEURO-TTR to Assess the Long-term Efficacy and Safety of Inotersen in Patients With Hereditary Transthyretin Amyloidosis (P1.324)
Brannagan, Thomas H., Wang, Annabel K., Coelho, Teresa , Polydefkis, Michael , Dyck, P. James B. , Scheinberg, Morton , Whelan, Carol , Drachman, Brian, Gorevic, Peter D., Monia, Brett P. , Hughes, Steven G. , Kwoh, Jesse, McEvoy, Bradley, Ackermann, Elizabeth J., Benson, Merrill D., Waddington‐Cruz, Márcia , Planté‐Bordeneuve, Violaine , Berk, John L. , Barroso, Fábio , Adams, David , Merlini, Giampaolo , Heitner, Stephen B. , Conceição, Isabel , Schmidt, Hartmut , Vita, Giuseppe , Gámez, Josep , Baker, Brenda F. , Gertz, Morie A.
Neurology | December 7, 2023 | Volume: 90 | Issue: 15_supplement | Pages: No page available
Safety and Efficacy of Inotersen in Patients With Hereditary Transthyretin Amyloidosis With Polyneuropathy (NEURO-TTR) (N2.001)
Wang, Annabel K., Coelho, Teresa , Polydefkis, Michael , Dyck, P. James B. , Scheinberg, Morton , Brannagan, Thomas H., Whelan, Carol , Drachman, Brian, Schmidt, Harmut, Gane, Edward , Gorevic, Peter D., Monia, Brett P. , Hughes, Steven G. , Kwoh, Jesse, McEvoy, Bradley, Ackermann, Elizabeth J., Benson, Merrill D., Gertz, Morie A. , Waddington‐Cruz, Márcia , Planté‐Bordeneuve, Violaine , Berk, John L. , Barroso, Fábio , Adams, David , Merlini, Giampaolo , Heitner, Stephen B. , Conceição, Isabel , Vita, Giuseppe , Gámez, Josep , Oliveira, Acary Souza Bulle de , Baker, Brenda F.
Neurology | December 7, 2023 | Volume: 90 | Issue: 15_supplement | Pages: No page available
Association of Variants in the SPTLC1 Gene With Juvenile Amyotrophic Lateral Sclerosis
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JAMA Neurology | August 30, 2021 | Volume: 78 | Issue: 10 | Pages: 1236
Inotersen Treatment for Patients with Hereditary Transthyretin Amyloidosis
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New England Journal of Medicine | July 4, 2018 | Volume: 379 | Issue: 1 | Pages: 22-31