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Marler, Ronald

Mayo Clinic

Department of Comparative Medicine, Mayo Clinic, Scottsdale, AZ 85259, USA.

Citations 1

Curative ex vivo liver-directed gene therapy in a pig model of hereditary tyrosinemia type 1
Mao, Shennen A. , Glorioso, Jaime , Elgilani, Faysal, Amiot, Bruce , Chen, Harvey , Rinaldo, Piero, Marler, Ronald J., Jiang, Huailei , DeGrado, Timothy R. , Suksanpaisan, Lukkana , O’Connor, Michael K. , Freeman, Brittany L., Ibrahim, Samar H. , Peng, Kah Whye, Grompe, Markus , Ikeda, Yasuhiro , Lillegard, Joseph B. , Russell, Stephen J. , Nyberg, Scott L. , Hickey, Raymond D, Marler, Ronald, O'Connor, Michael K, Hickey, Raymond , Harding, Cary O. , Ho, Chak‐Sum , Russell, Stephen J , Ibrahim, Samar H , Mao, Shennen A , Jiang, Huailei

Science Translational Medicine | July 27, 2016 | Volume: 8 | Issue: 349 | Pages: No page available

10.1126/scitranslmed.aaf3838 Get It

Transplantation of gene-corrected autologous hepatocytes can cure metabolic disease in a preclinical pig model of hereditary tyrosinemia type 1.