Citations 41
Inotersen Improves Norfolk Quality of Life-Diabetic Neuropathy Measures in Patients With Hereditary Transthyretin Amyloidosis with Polyneuropathy in the Phase 3 Study NEURO-TTR (S5.006)
Polydefkis, Michael , Coelho, Teresa , Dyck, P. James B. , Scheinberg, Morton , Brannagan, Thomas H., Whelan, Carol , Drachman, Brian, Gane, Edward , Gorevic, Peter D., Monia, Brett P. , Hughes, Steven G. , Kwoh, Jesse, McEvoy, Bradley, Ackermann, Elizabeth J., Benson, Merrill D., Wang, Annabel K., Waddington‐Cruz, Márcia , Planté‐Bordeneuve, Violaine , Berk, John L. , Barroso, Fábio , Adams, David , Merlini, Giampaolo , Heitner, Stephen B. , Conceição, Isabel , Schmidt, Hartmut , Vita, Giuseppe , Gámez, Josep , Oliveira, Acary Souza Bulle de , Baker, Brenda F. , Gertz, Morie A.
Neurology | December 7, 2023 | Volume: 90 | Issue: 15_supplement | Pages: No page available
Evaluation of Quality of Life and Disability in Patients with Hereditary Transthyretin-Mediated (hATTR) Amyloidosis with Polyneuropathy Following Treatment with Patisiran, An Investigational RNAi Therapeutic: Results from the Phase 3 APOLLO Study (S31.003)
O’Riordan, William, Yamashita, Taro , Kristen, Arnt V. , Tournev, Ivaylo, Coelho, Teresa , Lin, Kong-Ping, Dyck, P. James B. , Gandhi, Pritesh J., Sweetser, Marianne T., Goyal, Sunita , Gollob, Jared , Adams, David , González-Duarte, Alejandra , Yang, Chih‐Chao , Schmidt, Hartmut , Berk, John L. , Chen, Jihong , Goyal, Sunita, Suhr, Ole B.
Neurology | December 7, 2023 | Volume: 90 | Issue: 15_supplement | Pages: No page available
Burden of Hereditary Transthyretin Amyloidosis With Polyneuropathy in Patients Enrolled in the Phase 3 Study NEURO-TTR (P1.331)
Wang, Annabel K., Coelho, Teresa , Polydefkis, Michael , Dyck, P. James B. , Scheinberg, Morton , Brannagan, Thomas H., Whelan, Carol , Drachman, Brian, Gane, Edward , Gorevic, Peter D., Monia, Brett P. , Hughes, Stephen G. , Kwoh, Jesse, McEvoy, Bradley, Ackermann, Elizabeth J., Guthrie, Spencer , Benson, Merrill D., Berk, John L. , Waddington‐Cruz, Márcia , Planté‐Bordeneuve, Violaine , Barroso, Fábio , Adams, David , Heitner, Stephen B. , Conceição, Isabel , Schmidt, Hartmut , Vita, Giuseppe , Gámez, Josep , Oliveira, Acary Souza Bulle de , Hughes, Stephen G., Baker, Brenda F. , Kessler, Asia Sikora , Gertz, Morie A. , Merlini, Giampaolo
Neurology | December 7, 2023 | Volume: 90 | Issue: 15_supplement | Pages: No page available
Open Label Extension of the Phase 3 Study NEURO-TTR to Assess the Long-term Efficacy and Safety of Inotersen in Patients With Hereditary Transthyretin Amyloidosis (P1.324)
Brannagan, Thomas H., Wang, Annabel K., Coelho, Teresa , Polydefkis, Michael , Dyck, P. James B. , Scheinberg, Morton , Whelan, Carol , Drachman, Brian, Gorevic, Peter D., Monia, Brett P. , Hughes, Steven G. , Kwoh, Jesse, McEvoy, Bradley, Ackermann, Elizabeth J., Benson, Merrill D., Waddington‐Cruz, Márcia , Planté‐Bordeneuve, Violaine , Berk, John L. , Barroso, Fábio , Adams, David , Merlini, Giampaolo , Heitner, Stephen B. , Conceição, Isabel , Schmidt, Hartmut , Vita, Giuseppe , Gámez, Josep , Baker, Brenda F. , Gertz, Morie A.
Neurology | December 7, 2023 | Volume: 90 | Issue: 15_supplement | Pages: No page available
Safety and Efficacy of Inotersen in Patients With Hereditary Transthyretin Amyloidosis With Polyneuropathy (NEURO-TTR) (N2.001)
Wang, Annabel K., Coelho, Teresa , Polydefkis, Michael , Dyck, P. James B. , Scheinberg, Morton , Brannagan, Thomas H., Whelan, Carol , Drachman, Brian, Schmidt, Harmut, Gane, Edward , Gorevic, Peter D., Monia, Brett P. , Hughes, Steven G. , Kwoh, Jesse, McEvoy, Bradley, Ackermann, Elizabeth J., Benson, Merrill D., Gertz, Morie A. , Waddington‐Cruz, Márcia , Planté‐Bordeneuve, Violaine , Berk, John L. , Barroso, Fábio , Adams, David , Merlini, Giampaolo , Heitner, Stephen B. , Conceição, Isabel , Vita, Giuseppe , Gámez, Josep , Oliveira, Acary Souza Bulle de , Baker, Brenda F.
Neurology | December 7, 2023 | Volume: 90 | Issue: 15_supplement | Pages: No page available
Patisiran, an Investigational RNAi Therapeutic for Patients with Hereditary Transthyretin-Mediated (hATTR) Amyloidosis with Polyneuropathy: Results from the Phase 3 APOLLO study (CT.001)
O’Riordan, William, Yamashita, Taro , Kristen, Arnt V. , Tournev, Ivaylo, Coelho, Teresa , Lin, Kon‐Ping, Dyck, P. James B. , Gandhi, Pritesh J., Sweetser, Marianne T., Goyal, Sunita , Gollob, Jared , Adams, David , González-Duarte, Alejandra , Yang, Chih‐Chao , Schmidt, Hartmut , Berk, John L. , Lin, Kon‐Ping, Chen, Jihong , Goyal, Sunita, Suhr, Ole B.
Neurology | December 7, 2023 | Volume: 90 | Issue: 15_supplement | Pages: No page available
Long-Term Efficacy and Safety of Inotersen for Hereditary Transthyretin Amyloidosis: NEURO-TTR Open-Label Extension 2-Year Update (S27.008)
Brannagan, Thomas H., Wang, Annabel K., Polydefkis, Michael , Dyck, P. James B. , Khella, Sami, Hughes, Steven G. , Kwoh, Jesse, Jung, Shiangtung W., Guthrie, Spencer , Pollock, Michael, Benson, Merrill D., Coelho, Teresa , Waddington‐Cruz, Márcia , Planté‐Bordeneuve, Violaine , Berk, John L. , Barroso, Fábio , Merlini, Giampaolo , Conceição, Isabel , Gertz, Morie A.
Neurology | December 7, 2023 | Volume: 92 | Issue: 15_supplement | Pages: No page available
Responsiveness of Neuropathy Symptom and Change (NSC) Score Components in Inotersen Treatment of Hereditary Transthyretin Amyloidosis Polyneuropathy (P3.9-060)
Dyck, P. James B. , Coelho, Teresa , Brannagan, Thomas H., Khella, Sami, Polydefkis, Michael , Kincaid, John C., Wiesman, Janice F. , Litchy, William J. , Ackermann, Elizabeth J., Jung, Shiangtung W., Guthrie, Spencer , Pollock, Michael, Waddington‐Cruz, Márcia , Karam, Chafic , Berk, John L. , Mauermann, Michelle L. , Baker, Brenda F.
Neurology | December 7, 2023 | Volume: 92 | Issue: 15_supplement | Pages: No page available
Identifying Mixed Phenotype: Evaluating the Presence of Polyneuropathy in Patients with Hereditary Transthyretin-Mediated Amyloidosis with Cardiomyopathy (240)
Merkel, Madeline, Grogan, Martha , Hawkins, Philip N. , Kristen, Arnt V. , Lin, Hollis, McManus, Anastasia, Powell, Christine, Vest, John, Karsten, Verena, Berk, John L. , Suhr, Ole B. , Powell, Christine, Vest, John, Judge, Daniel P.
Neurology | December 7, 2023 | Volume: 94 | Issue: 15_supplement | Pages: No page available
Patisiran Treatment in Patients with Transthyretin Cardiac Amyloidosis
Maurer, Mathew S. , Kale, Parag , Fontana, Marianna, Grogan, Martha , Gustafsson, Finn , Hung, Rebecca R. , Gottlieb, Robert , Sarswat, Nitasha , Sekijima, Yoshiki , Taylor, Mark , Kubánek, Miloš , Paleček, Tomáš , YU, WEN‐CHUNG, Simões, Marcus Vinı́cius , Poulsen, Steen Hvitfeldt , Perfetto, Federico , Solomon, Scott D. , Carli, Marcelo F. Di , Badri, Prajakta , White, Matthew T. , Yureneva, Elena, Sweetser, Marianne T., Jay, Patrick Y. , Garg, Pushkal, Vest, John, Mogensen, Jens , Klaassen, Sabine , Cárdenas‐Soto, Karla , Savarese, Gianluigi , Hasific, Selma , Gottlieb, Robert L , Damy, Thibaud , Tahara, Nobuhiro , Taylor, Mark S, Tsujita, Kenichi , Simões, Marcus, Fernandes, Fábio, Diemberger, Igor, Di Carli, Marcelo, Chen, Jihong , Garg, Pushkal P, Gillmore, Julian D , Poulsen, Steen Hvitfeldt , Gustafsson, Finn , Maurer, Mathew S , Fontana, Marianna , Berk, John L. , González-Duarte, Alejandra , Donal, Erwan , Tang, W.H. Wilson , Obici, Laura , Fernandes, Fábio Danziato , Diemberger, Igor , Solomon, Scott David , Chen, Jihong , Vest, John, Gillmore, Julian D.
New England Journal of Medicine | October 25, 2023 | Volume: 389 | Issue: 17 | Pages: 1553-1565