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Grompe, Markus

https://orcid.org/0000-0002-6616-4345

A5067712261 | I165690674

Mayo Clinic

Oregon Health & Science University

Citations 2

Curative ex vivo liver-directed gene therapy in a pig model of hereditary tyrosinemia type 1

Science Translational Medicine | July 27, 2016 | Volume: 8 | Issue: 349 | Pages: No page available

10.1126/scitranslmed.aaf3838 | PMID 27464750

Transplantation of gene-corrected autologous hepatocytes can cure metabolic disease in a preclinical pig model of hereditary tyrosinemia type 1.
Silent Tyrosinemia Type I Without Elevated Tyrosine or Succinylacetone Associated with Liver Cirrhosis and Hepatocellular Carcinoma

Human Mutation | July 11, 2016 | Volume: 37 | Issue: 10 | Pages: 1097-1105

10.1002/humu.23047 | PMID 27397503