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Ornelas, Loren

A5053564990 | I1282927834

Mayo Clinic

Cedars-Sinai Medical Center

Citations 1

Targeting RNA Foci in iPSC-Derived Motor Neurons from ALS Patients with a C9ORF72 Repeat Expansion

Science Translational Medicine | October 23, 2013 | Volume: 5 | Issue: 208 | Pages: No page available

10.1126/scitranslmed.3007529 | PMID 24154603

Antisense oligonucleotides can correct disease-specific phenotypes in cultured motor neurons differentiated from iPSCs derived from ALS patients with a C9ORF72 repeat expansion.