A Small Molecule Exploits Hidden Structural Features within the RNA Repeat Expansion That Causes c9ALS/FTD and Rescues Pathological Hallmarks
ACS Chemical Neuroscience | October 22, 2021 | Volume: 12 | Issue: 21 | Pages: 4076-4089
10.1021/acschemneuro.1c00470
| PMID 34677935